- Hope vs. hype: seeking truth in recent Prilenia headlines
- Mini brains grown in a dish shed light on Huntington’s disease and how we might treat it
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- Hereditary Disease Foundation (HDF) conference 2024 – Day 4
- Hereditary Disease Foundation (HDF) conference 2024 – Day 3
- Hereditary Disease Foundation (HDF) conference 2024 – Day 2
- Hereditary Disease Foundation (HDF) conference 2024 – Day 1
- Blue skies for Skyhawk: Positive news from Phase 1 trial for SKY-0515
- Buckle in: Gene therapy AMT-130 appears to slow down signs of Huntington’s disease in Phase I/II clinical trial
- Positive news from Wave Life Sciences SELECT-HD trial
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