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ARM's list includes programs facing regulatory challenges, such as uniQure's Huntington's disease gene therapy. But according to analysts, the ...Read more

This is all about a potential therapy for Huntington's disease, and God knows that one could use a few more potential therapies. I've written about ...Read more

... disease," said CEO Linda Marbán in a company release. If the cell therapy is ... Huntington's disease gene therapy, prompting ethical concerns.Read more

... Huntington's disease. Worse, the WSJ reported "[t]he official also said a Uniqure executive had mischaracterized the FDA's request for how to ...Read more

Huntington's disease is a genetic neurodegenerative disorder that is life-threatening. It can result in symptoms like difficulty swallowing, ...Read more

... Huntington's disease candidate. The one-time uniQure therapy is given directly into the brain through small holes in the skull. Now, Johnson is ...Read more

Huntington's Disease Therapeutics Conference 2026 – Day 2. ⏱️ 18 min read | HDBuzz is back with Day 2 of the 21st annual CHDI HD Therapeutics ...Read more

Deves's expertise includes launching therapies for neurological disorders, notably chorea in Huntington's disease. His previous roles at Teva ...Read more

uniQure and FDA Clash Over Regulatory Decision for Huntington's Disease Therapy: Report · Novo Nordisk Signs Deal with Hims & Hers. The decision ...Read more

... called the FDA's request for a sham surgery–controlled Phase 3 trial for uniQure's Huntington's disease gene therapy “bureaucratic idiocy.”Read more

Industry veteran brings more than 30 years of experience launching therapies for neurological diseases, including Huntington's disease, ...Read more

UniQure's gene therapy for Huntington's disease has been turned away by the CBER despite targeting a defined genetic cause, showing clinical ...Read more

... Huntington's disease gene therapy, AMT-130. Despite the massive single-day rally, Benzinga Edge's Stock Rankings tell a more complex story. The ...Read more

The man's murder case was not pursued in court after experts determined he was suffering from Huntington's Disease.Read more

For uniQure, this is big news. The company has spent years developing AMT-130, a one-time gene therapy for Huntington's disease — a rare, fatal ...Read more